His third example: Methylmalonic Acidemia was not about a vaccine for a virus, but a cure for a disease. He says a gene in the DNA is missing or malfunctioning ("lost or aberration") This gene causes an enzyme to be produced in the liver but due to the absence or malfunction of that gene the liver is not producing the enzyme. He said "We are now able to package this information in mRNA, with the goal of giving it as an infusion. And then having it go to the liver to replace that missing information"

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